Nytt läkemedel mot cystisk fibros godkänt i USA

Ett nytt läkemedel mot cystisk fibros har godkänts av den amerikanska läkemedelsmyndigheten FDA.

By Anders Göransson

January 3, 2025 11:12 AM

Cystisk fibros är en ärftlig och livslång sjukdom som leder till slembildning i halsen, försvårad andning, nedsatt lungfunktion och ofta för tidig död. Sjukdomen kopplas till mutationer i en gen som kodar för en kloridkanal och har fått namnet cystic fibrosis transmembrane regulator (CFTR). I Sverige lider cirka 700 personer av sjukdomen.

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Nytt läkemedel mot cystisk fibros godkänt i USA

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