Nytt läkemedel ska förenkla behandling av blödarsjuka

En ny typ av behandling mot hemofili, som bara behöver ges varannan månad, har godkänts av den amerikanska läkemedelsmyndigheten FDA.

By Anders Göransson

March 31, 2025 11:40 AM

Qfitlia (fitusiran), som utvecklats av franska Sanofi, är en behandling som hjälper till att förebygga blödningar. Godkännandet i USA gäller behandling av patienter från 12 år och uppåt som har hemofili A eller hemofili B, med eller utan faktor VIII- eller IX-hämmare.

Behandlingen ges subkutant en gång varannan månad, medan flera andra terapier ges veckovis. Förhoppningen är att det ska underlätta patienternas vardag.

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