Trögt för genterapi mot blödarsjuka – kan dumpas av bolaget

Roctavian, en genterapi mot blödarsjuka som sågs som ett medicinsk genombrott, har floppat kommersiellt. Nu planerar företaget bakom att avyttra läkemedlet från sin portfölj.

By Anders Göransson

October 31, 2025 10:07 AM

När Roctavian godkändes i Europa 2022 och i USA året därpå betraktades det som en vetenskaplig milstolpe, som Life Science Sweden tidigare rapporterat. För första gången fanns det en engångsbehandling som alternativ till återkommande intravenösa behandlingar för att förebygga blödningar hos patienter med svår hemofili A.

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